Delandistrogene moxeparvovec, sold under the brand nameElevidys, is a recombinant gene therapy used for the treatment ofDuchenne muscular dystrophy.3l lt is designed to deliver into thebody a gene that leads to production of Elevidys micro-dystrophinthat contains selected domains of the dystrophin protein present innormal muscle cells.3l lt is an adeno-associated virus vector-basedgene therapy that is given by intravenous infusion (slow injectioninto a vein).[1]
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